Introductory Chapter: β-Thalassemia | IntechOpen
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article - Cureus
Frontiers | New Insights Into Pathophysiology of β-Thalassemia
IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Β-Thalassemias | NEJM
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
β-Thalassemia | Genetics in Medicine
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Β-Thalassemias | NEJM
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